- Velaglucerase alfa for the management of type 1 Gaucher diseaseJennifer L Morris
Department of Pharmacy, Riley Hospital for Children at Indiana University Health, Indianapolis, Indiana 46202, USA
Clin Ther 34:259-71. 2012..Symptomatic patients with type 1 GD are treated with enzyme replacement therapy (ERT) to improve disease-induced effects on hemoglobin, platelets, and liver and spleen volume. Currently, several ERTs are available...