Research Topics
| Malcolm A SmithSummaryAffiliation: National Institutes of Health Country: USA Publications
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Detail Information
Publications
Initial testing (stage 1) of the polyamine analog PG11047 by the pediatric preclinical testing programMalcolm A Smith
Cancer Therapy Evaluation Program, NCI, Bethesda, Maryland 20892, USA
Pediatr Blood Cancer 57:268-74. 2011..The activity of PG11047 was evaluated against the PPTP's in vitro and in vivo panels...
Evaluation of arsenic trioxide by the pediatric preclinical testing program with a focus on Ewing sarcomaMalcolm A Smith
Cancer Therapy Evaluation Program, NCI, Bethesda, Maryland 20892, USA
Pediatr Blood Cancer 59:753-5. 2012..Arsenic trioxide did not induce significant differences in EFS distribution compared to control in any of the Ewing sarcoma xenografts studied, and no objective responses were observed...
Initial testing of the investigational NEDD8-activating enzyme inhibitor MLN4924 by the pediatric preclinical testing programMalcolm A Smith
Cancer Therapy Evaluation Program, NCI, Bethesda, Maryland 20892, USA
Pediatr Blood Cancer 59:246-53. 2012..NAE is an essential component of the NEDD8 conjugation pathway, controlling the activity of a subset of ubiquitin-proteasome system (UPS) E3 ligases, multiprotein complexes that transfer ubiquitin molecules to substrate proteins...
Role of independent data-monitoring committees in randomized clinical trials sponsored by the National Cancer InstituteM A Smith
Cancer Therapy Evaluation Program, National Cancer Institute, Bethesda, MD 20892, USA
J Clin Oncol 15:2736-43. 1997..To describe the rationale for independent data monitoring committees (DMCs) for National Cancer Institute (NCI)-sponsored phase III cooperative group clinical trials...
An overview of progress in childhood cancer survivalMalcolm Smith
Clinical Investigations Branch, Cancer Therapy Evaluation Program, National Cancer Institute, National Institutes of Health, MD 20892, USA
J Pediatr Oncol Nurs 21:160-4. 2004..The experts present at the work group, Moving the Research Agenda Forward for Children With Cancer, offered several possibilities for utilizing CCSS data in expanding research opportunities concerned with cancer survivorship...
Commentary on "European collaboration in trials of new agents for children with cancer" by Ablett et alMalcolm A Smith
Cancer Therapy Evaluation Program, NCI 6130, Executive Boulevard Room 7025 Bethesda, MD 20892, USA
Eur J Cancer 40:1893-5. 2004....
Double trouble: cancer in twinsMalcolm Smith
Cancer Therapy Evaluation Program, NCI, Bethesda, Maryland 20892, USA
Pediatr Blood Cancer 46:412-3. 2006
SK-NEP-1 and Rh1 are Ewing family tumor linesMalcolm A Smith
Cancer Therapy Evaluation Program, National Cancer Institute, Bethesda, Maryland, USA
Pediatr Blood Cancer 50:703-6. 2008..These examples illustrate the importance of molecularly characterizing pediatric preclinical models used for testing new agents...
Update on developmental therapeutics for acute lymphoblastic leukemiaMalcolm A Smith
Cancer Therapy Evaluation Program, National Cancer Institute, 6130 Executive Boulevard, Room 7025, Bethesda, MD 20892, USA
Curr Hematol Malig Rep 4:175-82. 2009....
Secondary leukemia or myelodysplastic syndrome after treatment with epipodophyllotoxinsM A Smith
National Cancer Institute, Bethesda, MD 20892, USA
J Clin Oncol 17:569-77. 1999..The Cancer Therapy Evaluation Program (CTEP) of the National Cancer Institute (NCI) has developed a monitoring plan to obtain reliable estimates of the risk of secondary leukemia after epipodophyllotoxin treatment...
Trends in reported incidence of primary malignant brain tumors in children in the United StatesM A Smith
Cancer Therapy Evaluation Program, Division of Cancer Treatment and Diagnosis, National Cancer Institute, Bethesda, MD, USA
J Natl Cancer Inst 90:1269-77. 1998....
Conduct of phase I trials in children with cancerM Smith
Cancer Therapy Evaluation Program, National Cancer Institute, Bethesda, MD 20892, USA
J Clin Oncol 16:966-78. 1998..Where possible, pediatric phase I trials also define the pharmacokinetic behavior of new agents in children...
Initial testing of JNJ-26854165 (Serdemetan) by the pediatric preclinical testing programMalcolm A Smith
Cancer Therapy Evaluation Program, NCI, Bethesda, Maryland, USA
Pediatr Blood Cancer 59:329-32. 2012..Objective responses were observed in 4 of 37 solid tumor xenografts, and 2 of 7 ALL xenografts achieved PR or CR. Responses were noted in xenografts with both mutant and wild-type p53...
Initial testing (stage 1) of mapatumumab (HGS-ETR1) by the pediatric preclinical testing programMalcolm A Smith
Cancer Therapy Evaluation Program, NCI, Bethesda, Maryland 20892, USA
Pediatr Blood Cancer 54:307-10. 2010..Mapatumumab induced significant differences in event-free survival distribution compared to controls in 9 of 37 evaluable solid tumor xenografts tested, but in none of the 8 ALL xenografts...
Stage 1 testing and pharmacodynamic evaluation of the HSP90 inhibitor alvespimycin (17-DMAG, KOS-1022) by the pediatric preclinical testing programMalcolm A Smith
Cancer Therapy Evaluation Program, NCI, Bethesda, Maryland
Pediatr Blood Cancer 51:34-41. 2008..Alvespimycin (17-DMAG, KOS-1022), a potent small-molecule inhibitor of the protein chaperone Hsp90, is being developed as an anticancer agent because of the multiple Hsp90 client proteins involved in cancer cell growth and survival...
Design issues of randomized phase II trials and a proposal for phase II screening trialsLawrence V Rubinstein
Cancer Therapy Evaluation Program, National Cancer Institute, Bethesda, MD, USA
J Clin Oncol 23:7199-206. 2005....
Clinical trials referral resource. Current clinical trials of imatinib mesylateAnthony J Murgo
National Cancer Institute, Bethesda, MD, USA
Oncology (Williston Park) 17:513, 518, 521 passim. 2003
Tissue collection for correlative studies in childhood cancer clinical trials: ethical considerations and special imperativesBarry D Anderson
National Cancer Institute, Cancer Therapy Evaluation Program, Rockville, MD 20892 7436, USA
J Clin Oncol 22:4846-50. 2004....
microRNA profiling identifies cancer-specific and prognostic signatures in pediatric malignanciesJun S Wei
Oncogenomics Section, Pediatric Oncology Branch, Advanced Technology Center, National Cancer Institute, Gaithersburg, Maryland 20877, USA
Clin Cancer Res 15:5560-8. 2009..We therefore have performed expression profiles on a panel of pediatric tumors to identify cancer-specific microRNAs. We also investigated if microRNAs are coregulated with their host gene...
Clinical trials referral resource. Current clinical trials of molecularly targeted agents in children with cancerMalcolm A Smith
National Cancer Institute, USA
Oncology (Williston Park) 16:328, 331-3, 338 passim. 2002
Outcomes for children and adolescents with cancer: challenges for the twenty-first centuryMalcolm A Smith
Cancer Therapy Evaluation Program, National Cancer Institute, Bethesda, MD 20892, USA
J Clin Oncol 28:2625-34. 2010..This report provides an overview of current childhood cancer statistics to facilitate analysis of the impact of past research discoveries on outcome and provide essential information for prioritizing future research directions...
The Anti-CD19 Antibody-Drug Conjugate SAR3419 Prevents Hematolymphoid Relapse Postinduction Therapy in Preclinical Models of Pediatric Acute Lymphoblastic LeukemiaHernan Carol
Authors Affiliations Children s Cancer Institute Australia for Medical Research, University of New South Wales, Sydney, Australia Nationwide Children s Hospital, Columbus, Ohio and Cancer Therapy Evaluation Program, NCI, Bethesda, Maryland
Clin Cancer Res 19:1795-805. 2013..In this study, we evaluated the efficacy of SAR3419, an antibody-drug conjugate of the maytansinoid DM4 and a humanized anti-CD19 antibody, against B-cell precursor (BCP)-ALL and infant mixed lineage leukemia (MLL) xenografts...
Clinical trials refferal resource. Current clinical trials of new agents and novel therapies in pediatric leukemia and lymphomaMalcolm A Smith
National Cancer Institute, Bethesda, MD, USA
Oncology (Williston Park) 17:1377, 1380, 1383-4. 2003
Preliminary data release for randomized clinical trials of noninferiority: a new proposalEdward L Korn
Biometric Research Branch and Clinical Investigations Branch, Division of Cancer Treatment and Diagnosis, EPN 8128, National Cancer Institute, Bethesda, MD 20892, USA
J Clin Oncol 23:5831-6. 2005..Examples are given demonstrating how the proposal would work, along with a discussion of possible objections to the proposal...
Clinical trials referral resource. Current clinical trials of molecularly targeted agents in children with cancer, Part 2Malcolm A Smith
National Cancer Institute, USA
Oncology (Williston Park) 16:474, 479-80, 483-4 passim. 2002
Credentialing preclinical pediatric xenograft models using gene expression and tissue microarray analysisCraig C Whiteford
Oncogenomics Section, Comparative Oncology Program, and Cell and Molecular Biology Section, Pediatric Oncology Branch
Cancer Res 67:32-40. 2007..The database will facilitate the identification of tumor markers predictive of response to tested agents as well as the discovery of new molecular targets...
Initial testing (stage 1) of sunitinib by the pediatric preclinical testing programJohn M Maris
Children s Hospital of Philadelphia, University of Pennsylvania School of Medicine and Abramson Family Cancer Research Institute, Philadelphia, Pennsylvania, USA
Pediatr Blood Cancer 51:42-8. 2008..Sunitinib is an orally bioavailable, multi-targeted tyrosine kinase inhibitor with selectivity for PDGF receptors, VEGF receptors, FLT3, and KIT...
Molecular characterization of the pediatric preclinical testing panelGeoffrey Neale
Hartwell Center of Bioinformatics and Biotechnology, St Jude Children s Research Hospital, Memphis, Tennessee 38105, USA
Clin Cancer Res 14:4572-83. 2008..Identifying novel therapeutic agents for the treatment of childhood cancers requires preclinical models that recapitulate the molecular characteristics of their respective clinical histotypes...
Early average change in tumor size in a phase 2 trial: efficient endpoint or false promise?Larry V Rubinstein
J Natl Cancer Inst 99:1422-3. 2007
Study design and cohort characteristics of the Childhood Cancer Survivor Study: a multi-institutional collaborative projectLeslie L Robison
Department of Pediatrics, University of Minnesota, Minneapolis, Minnesota
Med Pediatr Oncol 38:229-39. 2002..It serves as a resource for addressing important issues such as risk of second malignancies, endocrine and reproductive outcome, cardiopulmonary complications, and psychosocial implications, among this unique and ever-growing population...
Initial testing of cisplatin by the pediatric preclinical testing programMimi Tajbakhsh
Children s Cancer Institute Australia for Medical Research, Randwick, New South Wales, Australia
Pediatr Blood Cancer 50:992-1000. 2008..Cisplatin is one of the most widely used drugs for the treatment of solid tumors in adults and children. Here, we report the activity of cisplatin against the PPTP panels of childhood cancer xenografts...
Testing of new agents in childhood cancer preclinical models: meeting summaryPeter J Houghton
St. Jude Children's Research Hospital, Memphis, Tennessee 38101, USA
Clin Cancer Res 8:3646-57. 2002..This report is a synthesis of the workshop's presentations and discussions...
Initial testing (stage 1) of the proteasome inhibitor bortezomib by the pediatric preclinical testing programPeter J Houghton
St Jude Children s Research Hospital, Memphis, Tennessee, USA
Pediatr Blood Cancer 50:37-45. 2008..The purpose of the current study was to evaluate the antitumor activity of bortezomib against the in vitro and in vivo childhood cancer preclinical models of the Pediatric Preclinical Testing Program (PPTP)...
A window on reality?Malcolm A Smith
J Clin Oncol 22:1360-2. 2004
The pediatric preclinical testing program: description of models and early testing resultsPeter J Houghton
Department of Molecular Pharmacology, St Jude Children s Research Hospital, Memphis, Tennessee 38105, USA
Pediatr Blood Cancer 49:928-40. 2007..Here, we describe the characteristics of the in vivo tumor panels and report results for the in vivo evaluation of two standard agents, vincristine and cyclophosphamide...
Initial testing of the VEGFR inhibitor AZD2171 by the pediatric preclinical testing programJohn M Maris
Children s Hospital of Philadelphia, University of Pennsylvania School of Medicine and Abramson Family Cancer Research Institute, Philadelphia, Pennsylvania, USA
Pediatr Blood Cancer 50:581-7. 2008..This study was designed to screen for antitumor activity of AZD2171 against the in vitro and in vivo childhood cancer preclinical models of the Pediatric Preclinical Testing Program (PPTP)...
Initial testing (stage 1) of a monoclonal antibody (SCH 717454) against the IGF-1 receptor by the pediatric preclinical testing programE Anders Kolb
Albert Einstein College of Medicine, The Children s Hospital at Montefiore, Bronx, New York, USA
Pediatr Blood Cancer 50:1190-7. 2008..The activity of SCH 717454 was evaluated against the in vitro and in vivo panels of the Pediatric Preclinical Testing Program (PPTP)...
Initial testing (stage 1) of the BH3 mimetic ABT-263 by the pediatric preclinical testing programRichard Lock
Children s Cancer Institute Australia for Medical Research, Randwick, NSW, Australia
Pediatr Blood Cancer 50:1181-9. 2008....
Initial testing of dasatinib by the pediatric preclinical testing programE Anders Kolb
The Children s Hospital at Montefiore, Bronx, New York, USA
Pediatr Blood Cancer 50:1198-206. 2008..Dasatinib, a dual inhibitor of the src and abl tyrosine kinases, was recently approved by the Federal Drug Administration for the treatment of imatinib mesylate-resistant chronic myeloid leukemia...
Initial testing (stage 1) of the mTOR inhibitor rapamycin by the pediatric preclinical testing programPeter J Houghton
St Jude Children s Research Hospital, Memphis, Tennessee, USA
Pediatr Blood Cancer 50:799-805. 2008..Here we report the activity of rapamycin against the in vitro and in vivo panels of the Pediatric Preclinical Testing Program (PPTP)...
Initial testing of VNP40101M (Cloretazine) by the pediatric preclinical testing programStephen T Keir
Preston Robert Tisch Brain Tumor Center, Duke University Medical Center, Durham, North Carolina 27710, USA
Pediatr Blood Cancer 51:439-41. 2008..VNP4010M antitumor activity was observed only in the absence of MGMT expression, with resistance to VNP4010M seen even with low MGMT expression...
