Research Topics
Species | Nicholas A DiProsperoSummaryAffiliation: National Institutes of Health Country: USA Publications
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Detail Information
Publications
Neurological effects of high-dose idebenone in patients with Friedreich's ataxia: a randomised, placebo-controlled trialNicholas A Di Prospero
Neurogenetics Branch, National Institute of Neurological Disorders and Stroke, National Institutes of Health, Bethesda, MD 20892 3705, USA
Lancet Neurol 6:878-86. 2007..Previous studies have indicated that the antioxidant idebenone (5 mg/kg daily) reduces cardiac hypertrophy, but definite improvement in neurological function has not been shown...
Early changes in Huntington's disease patient brains involve alterations in cytoskeletal and synaptic elementsNicholas A DiProspero
Neurogenetics Branch, National Institute of Neurological Disorders and Stroke, NIH, 9000 Rockville Pike, Bethesda, MD 20892, USA
J Neurocytol 33:517-33. 2004..We propose that mutant huntingtin affects proteins involved in synaptic function and cytoskeletal integrity before symptoms develop which may influence early disease onset and/or progression...
Therapeutics development for triplet repeat expansion diseasesNicholas A Di Prospero
Neurogenetics Branch, National Institute of Neurological Disorders and Stroke, National Institutes of Health, Bethesda, Maryland 20892 3705, USA
Nat Rev Genet 6:756-65. 2005..Examination of experimental findings reveals similarities in disease mechanisms as well as possibilities for treatment...
Safety, tolerability, and pharmacokinetics of high-dose idebenone in patients with Friedreich ataxiaNicholas A Di Prospero
Neurogenetics Branch, National Institute of Neurological Disorders and Stroke, National Institutes of Health, Bethesda, MD 20892 3705, USA
Arch Neurol 64:803-8. 2007..Some studies suggest that higher doses of idebenone may be more effective, but pharmacology and toxicology at higher doses have not been investigated in human beings...
PACSIN 1 interacts with huntingtin and is absent from synaptic varicosities in presymptomatic Huntington's disease brainsJan Modregger
Institute for Biochemistry II, University of Cologne, D 50931 Cologne, Germany
Hum Mol Genet 11:2547-58. 2002....
HDAC6 rescues neurodegeneration and provides an essential link between autophagy and the UPSUdai Bhan Pandey
Department of Neurology, University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania 19104, USA
Nature 447:859-63. 2007..Morover, these findings suggest that it may be possible to intervene in neurodegeneration by augmenting HDAC6 to enhance autophagy...
Phosphorylation of profilin by ROCK1 regulates polyglutamine aggregationJieya Shao
Departments of Neurology and Cellular and Molecular Pharmacology, UCSF, San Francisco, California 94143, USA
Mol Cell Biol 28:5196-208. 2008..A signaling pathway from ROCK1 to profilin thus controls polyglutamine protein aggregation and is targeted by a promising therapeutic lead for HD...
