A J McVie WylieSummaryAffiliation: Genzyme Corporation Country: USA Publications
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Publications
Biochemical and pharmacological characterization of different recombinant acid alpha-glucosidase preparations evaluated for the treatment of Pompe diseaseA J McVie-Wylie
Biologics Research and Development, Genzyme Corporation, One Mountain Road, Framingham, MA 01701, USA
Mol Genet Metab 94:448-55. 2008....
Long-term efficacy after [E1-, polymerase-] adenovirus-mediated transfer of human acid-alpha-glucosidase gene into glycogen storage disease type II knockout miceE Y Ding
Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27710, USA
Hum Gene Ther 12:955-65. 2001..The results suggest that gene therapy strategies may have the potential to significantly improve the clinical course for GSD-II patients...
Multiple muscles in the AMD quail can be "cross-corrected" of pathologic glycogen accumulation after intravenous injection of an [E1-, polymerase-] adenovirus vector encoding human acid-alpha-glucosidaseA J McVie-Wylie
Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27710, USA
J Gene Med 5:399-406. 2003....
