Johanna H van der Lee

Summary

Affiliation: Academic Medical Center
Country: The Netherlands

Publications

  1. pmc Sample size calculations in pediatric clinical trials conducted in an ICU: a systematic review
    Stavros Nikolakopoulos
    Department of Biostatistics, Julius Center for Health Sciences and Primary Care, University Medical Center Utrecht, Str, 6, 131, PO Box 85500, 3508 Utrecht, GA, The Netherlands
    Trials 15:274. 2014
  2. pmc Insufficient evidence for the use of a physical examination to detect maltreatment in children without prior suspicion: a systematic review
    Eva Mm Hoytema van Konijnenburg
    Department of Paediatrics, Emma Children s Hospital Academic Medical Centre, University of Amsterdam, Postbus 22660, Amsterdam, 1100 DD, The Netherlands
    Syst Rev 2:109. 2013
  3. pmc Pharmacokinetics and pharmacodynamics of medication in asphyxiated newborns during controlled hypothermia. The PharmaCool multicenter study
    Timo R de Haan
    Department of Neonatology, Emma Children s Hospital, Academic Medical Center, Amsterdam, The Netherlands
    BMC Pediatr 12:45. 2012
  4. ncbi request reprint Clinimetric properties of the motor activity log for the assessment of arm use in hemiparetic patients
    J H van der Lee
    Department of Rehabilitation Medicine, VU University Medical Center, Amsterdam, The Netherlands
    Stroke 35:1410-4. 2004
  5. ncbi request reprint Definitions and measurement of chronic health conditions in childhood: a systematic review
    Johanna H van der Lee
    Department of Pediatric Clinical Epidemiology, Emma Children s Hospital, Academic Medical Center, Amsterdam, The Netherlands
    JAMA 297:2741-51. 2007
  6. ncbi request reprint Efficient ways exist to obtain the optimal sample size in clinical trials in rare diseases
    J H van der Lee
    Department of Pediatric Clinical Epidemiology, Emma Children s Hospital, Academic Medical Center, University of Amsterdam, Meibergdreef 9, 1105 AZ Amsterdam, The Netherlands
    J Clin Epidemiol 61:324-30. 2008
  7. pmc Pitfalls in the design and analysis of paediatric clinical trials: a case of a 'failed' multi-centre study, and potential solutions
    Johanna H van der Lee
    Department of Paediatric Clinical Epidemiology, Emma Children s Hospital, Academic Medical Centre, University of Amsterdam, The Netherlands
    Acta Paediatr 98:385-91. 2009
  8. ncbi request reprint Sequential design with boundaries approach in pediatric intervention research reduces sample size
    Johanna H van der Lee
    Department of Pediatric Clinical Epidemiology, Emma Children s Hospital, Academic Medical Center, University of Amsterdam, 1105 AZ Amsterdam, The Netherlands
    J Clin Epidemiol 63:19-27. 2010
  9. pmc A systematic review of the reporting of Data Monitoring Committees' roles, interim analysis and early termination in pediatric clinical trials
    Ricardo M Fernandes
    Departamento da Crianca e da Familia, Hospital de Santa Maria, Centro Hospitalar Lisboa Norte EPE, Laboratorio de Farmacologia Clinica e Terapeutica, Instituto de Medicina Molecular, Faculdade de Medicina, Universidade de Lisboa, Portugal
    BMC Pediatr 9:77. 2009
  10. ncbi request reprint Defining chronic diseases and health conditions in childhood (0-18 years of age): national consensus in the Netherlands
    Lidwine B Mokkink
    Psychosocial Department, Emma Children s Hospital, Academic Medical Centre, University of Amsterdam, Amsterdam, The Netherlands
    Eur J Pediatr 167:1441-7. 2008

Collaborators

Detail Information

Publications23

  1. pmc Sample size calculations in pediatric clinical trials conducted in an ICU: a systematic review
    Stavros Nikolakopoulos
    Department of Biostatistics, Julius Center for Health Sciences and Primary Care, University Medical Center Utrecht, Str, 6, 131, PO Box 85500, 3508 Utrecht, GA, The Netherlands
    Trials 15:274. 2014
    ..Researchers should be aware of the importance of nuisance parameters in study design and in the interpretation of the results. ..
  2. pmc Insufficient evidence for the use of a physical examination to detect maltreatment in children without prior suspicion: a systematic review
    Eva Mm Hoytema van Konijnenburg
    Department of Paediatrics, Emma Children s Hospital Academic Medical Centre, University of Amsterdam, Postbus 22660, Amsterdam, 1100 DD, The Netherlands
    Syst Rev 2:109. 2013
    ..This article aims to evaluate the diagnostic value of a complete physical examination as a screening instrument to detect maltreatment in children without prior suspicion...
  3. pmc Pharmacokinetics and pharmacodynamics of medication in asphyxiated newborns during controlled hypothermia. The PharmaCool multicenter study
    Timo R de Haan
    Department of Neonatology, Emma Children s Hospital, Academic Medical Center, Amsterdam, The Netherlands
    BMC Pediatr 12:45. 2012
    ..This multicenter observational cohort study was designed to answer the question how hypothermia influences the distribution, metabolism and elimination of commonly used drugs in neonatal intensive care...
  4. ncbi request reprint Clinimetric properties of the motor activity log for the assessment of arm use in hemiparetic patients
    J H van der Lee
    Department of Rehabilitation Medicine, VU University Medical Center, Amsterdam, The Netherlands
    Stroke 35:1410-4. 2004
    ....
  5. ncbi request reprint Definitions and measurement of chronic health conditions in childhood: a systematic review
    Johanna H van der Lee
    Department of Pediatric Clinical Epidemiology, Emma Children s Hospital, Academic Medical Center, Amsterdam, The Netherlands
    JAMA 297:2741-51. 2007
    ..To obtain valid and reliable estimates of the prevalence of chronic health conditions, a clear definition is needed...
  6. ncbi request reprint Efficient ways exist to obtain the optimal sample size in clinical trials in rare diseases
    J H van der Lee
    Department of Pediatric Clinical Epidemiology, Emma Children s Hospital, Academic Medical Center, University of Amsterdam, Meibergdreef 9, 1105 AZ Amsterdam, The Netherlands
    J Clin Epidemiol 61:324-30. 2008
    ..The objective of this paper is to give an overview of design options to obtain a statistically valid result while including a minimum number of subjects...
  7. pmc Pitfalls in the design and analysis of paediatric clinical trials: a case of a 'failed' multi-centre study, and potential solutions
    Johanna H van der Lee
    Department of Paediatric Clinical Epidemiology, Emma Children s Hospital, Academic Medical Centre, University of Amsterdam, The Netherlands
    Acta Paediatr 98:385-91. 2009
    ....
  8. ncbi request reprint Sequential design with boundaries approach in pediatric intervention research reduces sample size
    Johanna H van der Lee
    Department of Pediatric Clinical Epidemiology, Emma Children s Hospital, Academic Medical Center, University of Amsterdam, 1105 AZ Amsterdam, The Netherlands
    J Clin Epidemiol 63:19-27. 2010
    ..To estimate the difference between the number of subjects actually included in pediatric sequential trials and the sample size that would have been included with a fixed-sample design...
  9. pmc A systematic review of the reporting of Data Monitoring Committees' roles, interim analysis and early termination in pediatric clinical trials
    Ricardo M Fernandes
    Departamento da Crianca e da Familia, Hospital de Santa Maria, Centro Hospitalar Lisboa Norte EPE, Laboratorio de Farmacologia Clinica e Terapeutica, Instituto de Medicina Molecular, Faculdade de Medicina, Universidade de Lisboa, Portugal
    BMC Pediatr 9:77. 2009
    ..Our aim was to evaluate the frequency and quality of the reporting on DMC composition and roles, interim analysis and early termination in pediatric trials...
  10. ncbi request reprint Defining chronic diseases and health conditions in childhood (0-18 years of age): national consensus in the Netherlands
    Lidwine B Mokkink
    Psychosocial Department, Emma Children s Hospital, Academic Medical Centre, University of Amsterdam, Amsterdam, The Netherlands
    Eur J Pediatr 167:1441-7. 2008
    ..By this systematic and thorough procedure, national consensus on a comprehensive definition of chronic conditions in children which can be used for epidemiological research was reached...
  11. ncbi request reprint Improving the Action Research Arm test: a unidimensional hierarchical scale
    Johanna H van der Lee
    Department of Rehabilitation Medicine, VU University Medical Center, Amsterdam, The Netherlands
    Clin Rehabil 16:646-53. 2002
    ..The Action Research Arm (ARA) test is a performance test of upper extremity motor function which consists of 19 items divided into four hierarchical subtests. This multidimensionality has not yet been tested empirically...
  12. pmc Capturing phenotypic heterogeneity in MPS I: results of an international consensus procedure
    Minke H de Ru
    Department of Paediatrics, Academic Medical Center, University Hospital of Amsterdam H7 270, Meibergdreef 9, 1105 AZ Amsterdam, The Netherlands
    Orphanet J Rare Dis 7:22. 2012
    ..Therefore, a numerical severity scale for classifying different MPS I phenotypes at diagnosis based on clinical signs and symptoms was developed...
  13. pmc Enzyme replacement therapy and/or hematopoietic stem cell transplantation at diagnosis in patients with mucopolysaccharidosis type I: results of a European consensus procedure
    Minke H de Ru
    Department of Pediatrics and Amsterdam Lysosome Center Sphinx, Academic Medical Center, University of Amsterdam, Amsterdam, The Netherlands
    Orphanet J Rare Dis 6:55. 2011
    ..A European consensus procedure was organized to reach consensus about the use of these two treatment strategies...
  14. ncbi request reprint Measuring mobility limitations in children with cerebral palsy: development, scalability, unidimensionality, and internal consistency of the mobility questionnaire, MobQues47
    Leo D Roorda
    Department of Rehabilitation Medicine, VU University Medical Center, Amsterdam, The Netherlands
    Arch Phys Med Rehabil 91:1194-209. 2010
    ....
  15. pmc Treatment of hip dysplasia in patients with mucopolysaccharidosis type I after hematopoietic stem cell transplantation: results of an international consensus procedure
    Eveline J Langereis
    Department of Pediatrics and Lysosome Center Sphinx, Academic Medical Center, University of Amsterdam, H7 270, Meibergdreef 9, 1105 AZ Amsterdam, The Netherlands
    Orphanet J Rare Dis 8:155. 2013
    ..Therefore, an international Delphi consensus procedure was initiated to construct consensus-based clinical practice guidelines in the absence of available evidence...
  16. ncbi request reprint Children of non-Western origin with end-stage renal disease in the Netherlands, Belgium and a part of Germany have impaired health-related quality of life compared with Western children
    Nikki J Schoenmaker
    Department of Paediatric Nephrology, Emma Children s Hospital Academic Medical Centre, Amsterdam, The Netherlands
    Nephrol Dial Transplant 29:448-57. 2014
    ..They have unfavourable somatic outcomes compared with ESRD children of Western origin. In this study, we compared the Health-related Quality of Life (HRQoL) of both groups...
  17. pmc Neonatal gram negative and Candida sepsis survival and neurodevelopmental outcome at the corrected age of 24 months
    Timo R de Haan
    Department of Neonatology, Emma Children s Hospital, Academic Medical Center Amsterdam, The Netherlands
    PLoS ONE 8:e59214. 2013
    ..To evaluate the long term neurodevelopmental outcome of premature infants exposed to either gram- negative sepsis (GNS) or neonatal Candida sepsis (NCS), and to compare their outcome with premature infants without sepsis...
  18. ncbi request reprint Quality and consistency of clinical practice guidelines for the management of children on chronic dialysis
    Nikki J Schoenmaker
    Department of Paediatric Nephrology, Emma Children s Hospital AMC, Amsterdam, The Netherlands
    Nephrol Dial Transplant 28:3052-61. 2013
    ..We aimed to identify all current published guidelines for the management of children on chronic dialysis, assess the quality of their development and evaluate consistency among their recommendations...
  19. ncbi request reprint Prognostic tests in term neonates with hypoxic-ischemic encephalopathy: a systematic review
    Henriette van Laerhoven
    Department of aNeonatology, Emma Children s Hospital, Academic Medical Center Amsterdam, Netherlands
    Pediatrics 131:88-98. 2013
    ..A reliable evidence-based prognosis is essential. The study goal was to investigate the prognostic value of currently used clinical tests in neonatal patients with perinatal asphyxia and HIE...
  20. ncbi request reprint State of the evidence on acute asthma management in children: a critical appraisal of systematic reviews
    Nicole Boluyt
    Emma Children s Hospital Department of Pediatric Clinical Epidemiology, Room H3 145, Academic Medical Center, PO Box 22700, 1100 DD Amsterdam, The Netherlands
    Pediatrics 120:1334-43. 2007
    ..Our goal was to evaluate clinical, methodologic, and reporting aspects of systematic reviews on the management of acute asthma in children...
  21. ncbi request reprint Development and validation of a pediatric severity index for sickle cell patients
    Xandra W van den Tweel
    Department of Pediatric Hematology, Emma Children s Hospital, Academic Medical Center, Amsterdam, The Netherlands
    Am J Hematol 85:746-51. 2010
    ..The validity and reliability of this index should be further evaluated in a prospective study including a larger cohort, preferably diagnosed at birth...
  22. ncbi request reprint Ultrastructural analysis of dermal fibroblasts in mucopolysaccharidosis type I: Effects of enzyme replacement therapy and hematopoietic cell transplantation
    Josanne Cox-Brinkman
    Department of Pediatrics, Academic Medical Center, Amsterdam, The Netherlands
    Ultrastruct Pathol 34:126-32. 2010
    ..In conclusion, both ERT and HCT are capable of restoring, at least partially, dermal fibroblast morphology in MPS I...
  23. ncbi request reprint Treating patients with hemiplegic shoulder pain
    Ingrid A K Snels
    Department of Rehabilitation Medicine, University Hospital, Vrije Universiteit, Amsterdam, The Netherlands
    Am J Phys Med Rehabil 81:150-60. 2002
    ..However, functional electrical stimulation and intra-articular triamcinolone acetonide injections seem to be the most promising treatment options...