Research Topics
| Björn HoffmannSummaryAffiliation: Heinrich Heine University Country: Germany Publications
| Collaborators |
Detail Information
Publications
Effects of enzyme replacement therapy on pain and health related quality of life in patients with Fabry disease: data from FOS (Fabry Outcome Survey)B Hoffmann
Department for General Pediatrics, University Children s Hospital, Heinrich Heine University Dusseldorf, Moorenstr 5, D 40225 Dusseldorf, Germany
J Med Genet 42:247-52. 2005..Symptoms often begin in childhood and include acroparaesthesia, with burning or tingling pain that spreads from the extremities to more proximal sites...
Fabry disease: recent advances in pathology, diagnosis, treatment and monitoringBjörn Hoffmann
Department for General Pediatrics, University Children s Hospital, Heinrich Heine University Dusseldorf, Germany
Orphanet J Rare Dis 4:21. 2009..This review aims to summarize recent developments and progress with high impact for Fabry disease...
Fabry disease-often seen, rarely diagnosedBjörn Hoffmann
Klinik fur Allgemeine Padiatrie, Universitatsklinikum Dusseldorf, Heinrich Heine Universitat, Dusseldorf, Germany
Dtsch Arztebl Int 106:440-7. 2009..Its clinical manifestations are very diverse, and its differential diagnosis is correspondingly broad. Thus, there is often a delay before the diagnosis of Fabry disease is established...
[Asthma during pregnancy]A Gillissen
Robert-Koch-Klinik, Thoraxzentrum des Klinikums St. Georg, Leipzig
Dtsch Med Wochenschr 133:1977-80. 2008
[Fabry disease - complex clinical picture, simple diagnosis procedure, causal treatment]B Hoffmann
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Dtsch Med Wochenschr 133:1965-72; quiz 1973-4. 2008
Nature and prevalence of pain in Fabry disease and its response to enzyme replacement therapy--a retrospective analysis from the Fabry Outcome SurveyBjoern Hoffmann
University Children s Hospital, Heinrich Heine University Duesseldorf, Germany
Clin J Pain 23:535-42. 2007..Fabry disease is a multisystemic life-threatening lysosomal storage disorder caused by deficiency of alpha-galactosidase A. Symptoms of the disease may occur in different organs including kidney, heart, and the nervous system...
Gastrointestinal symptoms in Fabry disease: everything is possible, including treatmentBjörn Hoffmann
University Children s Hospital, Heinrich Heine University, Dusseldorf, Germany
Acta Paediatr Suppl 96:84-6. 2007..CONCLUSION: Gastrointestinal symptoms in Fabry disease may have been underestimated. The FOS database supports previous reports of beneficial effects of enzyme replacement therapy on gastrointestinal symptoms in Fabry disease...
Acute neuronopathic Gaucher disease complicated by fatal gastrointestinal bleedingB Hoffmann
Department of General Pediatrics, University Children s Hospital, Heinrich Heine University Dusseldorf, Dusseldorf, Germany
Neuropediatrics 37:163-5. 2006..The gastric mucosa showed marked infiltration with Gaucher cells, in particular around the ulcer. Alterations of the gastrointestinal mucosa offer a new explanation for gastrointestinal bleedings in this disease...
Neurological manifestations in lysosomal storage disorders - from pathology to first therapeutic possibilitiesB Hoffmann
Department of General Paediatrics, University Children s Hospital, Heinrich Heine University Duesseldorf, Germany
Neuropediatrics 36:285-9. 2005....
[Situation of adult patients with inborn errors of metabolism. A survey in Germany]Björn Hoffmann
Klinik fur Allgemeine Padiatrie, Heinrich Heine Universitat, Dusseldorf
Med Klin (Munich) 100:617-23. 2005..Many patients have reached adulthood already, and thus may be attended by adult physicians. In this study the authors evaluated the situation of adult patients with metabolic diseases in Germany...
[Fabry disease--a provocation for pediatrics]B Hoffmann
Klinik fur Allgemeine Padiatrie, Heinrich Heine Universitat Dusseldorf
Klin Padiatr 218:38-40. 2006..Enzyme replacement therapy (ERT) offers an efficient treatment of Fabry disease. On the basis of newly diagnosed patients we describe the clinical picture, diagnosis and principles of ERT...
Longitudinal assessment of intellectual achievement in patients with classical galactosemiaPeter Schadewaldt
Deutsches Diabetes Zentrum, Abteilung Klinische Biochemie und Pathobiochemie, Auf m Hennekamp 65, D 40225 Dusseldorf, Germany
Pediatrics 125:e374-81. 2010..To conduct a longitudinal assessment of long-term cognitive outcome in patients with classical galactosemia...
Inborn errors of carbohydrate metabolismErtan Mayatepek
Department of General Pediatrics, University Children s Hospital, Moorenstrasse 5, 40225 Dusseldorf, Germany
Best Pract Res Clin Gastroenterol 24:607-18. 2010..A lactose-free infant formula can be life-saving in affected neonates whereas a strict fructose-restricted diet is indicated in hereditary fructose intolerance...
Traffic exposure and subclinical cardiovascular disease: is the association modified by socioeconomic characteristics of individuals and neighbourhoods? Results from a multilevel study in an urban regionN Dragano
Department of Medical Sociology, University of Duesseldorf, PO Box 10 10 07, D 40001 Duesseldorf, Germany
Occup Environ Med 66:628-35. 2009..We examined whether the association between long-term exposure to high traffic and early signs of coronary artery disease is modified by SES...
Living situation, occupation and health-related quality of life in adult patients with classic galactosemiaBjörn Hoffmann
Department of General Pediatrics, University Children s Hospital, Heinrich Heine University Dusseldorf, Dusseldorf, Germany
J Inherit Metab Dis 35:1051-8. 2012....
Impact of longitudinal plasma leucine levels on the intellectual outcome in patients with classic MSUDBjörn Hoffmann
Department of General Pediatrics, Heinrich Heine University, Duesseldorf, Germany
Pediatr Res 59:17-20. 2006..To achieve the best possible intellectual outcome for affected individuals, we recommend that in infants and preschool children the target range for plasma leucine should not exceed 200 micromol/L...
Hunter disease before and during enzyme replacement therapyBjörn Hoffmann
Department of General Pediatrics, University Children s Hospital, Heinrich Heine University, Dusseldorf, Germany
Pediatr Neurol 45:181-4. 2011..We conclude that all patients with mucopolysaccharidosis type II (those with and without clinical central nervous system involvement) may benefit from enzyme replacement therapy...
Cross-sectional analysis of speech and cognitive performance in 32 patients with classic galactosemiaBjörn Hoffmann
Department of General Pediatrics, University Children s Hospital, Heinrich Heine University Dusseldorf, Siegen, Germany
J Inherit Metab Dis 34:421-7. 2011..Moreover, speech impairment is common with conflicting reports regarding frequency, pattern, and relation to IQ...
Gastrointestinal symptoms in 342 patients with Fabry disease: prevalence and response to enzyme replacement therapyBjoern Hoffmann
Department of General Pediatrics, University Children s Hospital, Heinrich Heine University, Duesseldorf, Germany
Clin Gastroenterol Hepatol 5:1447-53. 2007....
Deficient alpha-galactosidase A activity in plasma but no Fabry disease--a pitfall in diagnosisBjoern Hoffmann
Clin Chem Lab Med 43:1276-7. 2005
