Research Topics
Genomes and Genes
| Bart L LoeysSummaryAffiliation: Ghent University Country: Belgium Publications
| Collaborators
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Detail Information
Publications
Aneurysm syndromes caused by mutations in the TGF-beta receptorBart L Loeys
McKusick Nathans Institute for Genetic Medicine, Johns Hopkins University School of Medicine, and the Kennedy Krieger Institute, Baltimore, USA
N Engl J Med 355:788-98. 2006....
The revised Ghent nosology for the Marfan syndromeBart L Loeys
Center for Medical Genetics, Ghent University Hospital, De Pintelaan 185, Gent, Belgium
J Med Genet 47:476-85. 2010..We anticipate that these new guidelines may delay a definitive diagnosis of MFS but will decrease the risk of premature or misdiagnosis and facilitate worldwide discussion of risk and follow-up/management guidelines...
Angiotensin II type 1 receptor blockade attenuates TGF-beta-induced failure of muscle regeneration in multiple myopathic statesRonald D Cohn
McKusick Nathans Institute of Genetic Medicine, Baltimore, Maryland 21205, USA
Nat Med 13:204-10. 2007..Moreover, we show TGF-beta-induced failure of muscle regeneration and a similar therapeutic response in a dystrophin-deficient mouse model of Duchenne muscular dystrophy...
Loss-of-function mutations in TGFB2 cause a syndromic presentation of thoracic aortic aneurysmMark E Lindsay
Helen B Taussig Children s Heart Center, Department of Pediatrics, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA
Nat Genet 44:922-7. 2012..Taken together, these data support the hypothesis that compensatory autocrine and/or paracrine events contribute to the pathogenesis of TGF-β-mediated vasculopathies...
Noncanonical TGFβ signaling contributes to aortic aneurysm progression in Marfan syndrome miceTammy M Holm
Howard Hughes Medical Institute and Institute of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, MD 21205, USA
Science 332:358-61. 2011..Thus, noncanonical (Smad-independent) TGFβ signaling is a prominent driver of aortic disease in MFS mice, and inhibition of the ERK1/2 or JNK1 pathways is a potential therapeutic strategy for the disease...
A syndrome of altered cardiovascular, craniofacial, neurocognitive and skeletal development caused by mutations in TGFBR1 or TGFBR2Bart L Loeys
McKusick Nathans Institute of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA
Nat Genet 37:275-81. 2005....
Altered TGFbeta signaling and cardiovascular manifestations in patients with autosomal recessive cutis laxa type I caused by fibulin-4 deficiencyMarjolijn Renard
Center for Medical Genetics, University Hospital Ghent, De Pintelaan 185, Ghent, Belgium
Eur J Hum Genet 18:895-901. 2010..This confirms the important role of fibulin-4 in vascular elastic fiber assembly. Furthermore, we provide the first evidence for the involvement of altered TGFbeta signaling in the pathogenesis of FBLN4 mutations in humans...
Mutations in the TGF-β repressor SKI cause Shprintzen-Goldberg syndrome with aortic aneurysmAlexander J Doyle
McKusick Nathans Institute of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA
Nat Genet 44:1249-54. 2012..These data support the conclusions that increased TGF-β signaling is the mechanism underlying SGS and that high signaling contributes to multiple syndromic presentations of aortic aneurysm...
Early surgical experience with Loeys-Dietz: a new syndrome of aggressive thoracic aortic aneurysm diseaseJason A Williams
Division of Cardiac Surgery, The Johns Hopkins Medical Institutions, Baltimore, Maryland 21287, USA
Ann Thorac Surg 83:S757-63; discussion S785-90. 2007..Our surgical experience with LDS was reviewed to assess outcomes and develop guidelines for management of this aggressive disease...
Comprehensive clinical and molecular assessment of 32 probands with congenital contractural arachnodactyly: report of 14 novel mutations and review of the literatureBert L Callewaert
Center for Medical Genetics, Ghent University Hospital, Belgium
Hum Mutat 30:334-41. 2009..Finally, the FBN2-negative patients in this cohort were clinically indistinguishable from all published FBN2-positive patients harboring a FBN2 mutation, suggesting locus heterogeneity...
Losartan, an AT1 antagonist, prevents aortic aneurysm in a mouse model of Marfan syndromeJennifer P Habashi
Howard Hughes Medical Institute and Department of Pediatrics, Johns Hopkins University School of Medicine, Baltimore, MD 21205, USA
Science 312:117-21. 2006....
Loeys-Dietz syndrome: MDCT angiography findingsPamela T Johnson
Russell H Morgan Department of Radiology and Radiological Science, Johns Hopkins School of Medicine, 601 N Caroline St, Rm 3251, Baltimore, MD 21287, USA
AJR Am J Roentgenol 189:W29-35. 2007..Serial imaging assessment by radiologists is an important component in the management of these patients...
Marfan syndrome: from gene to therapyNikhita Bolar
Laboratory for Aneurysmal Disease Research, Center for Medical Genetics, University of Antwerp and Antwerp University Hospital, Antwerp, Belgium
Curr Opin Pediatr 24:498-504. 2012....
Pseudoxanthoma elasticum-like phenotype with cutis laxa and multiple coagulation factor deficiency represents a separate genetic entityOlivier M Vanakker
Center for Medical Genetics, Ghent University Hospital, Ghent, Belgium
J Invest Dermatol 127:581-7. 2007..These findings all support the hypothesis that the disorder indeed represents a separate clinical and genetic entity, the molecular background of which remains to be unraveled...
Musculoskeletal findings of Loeys-Dietz syndromeGurkan Erkula
Department of Orthopaedic Surgery, Johns Hopkins Bayview Medical Center, 4940 Eastern Avenue, Baltimore, MD 21224 2780, USA
J Bone Joint Surg Am 92:1876-83. 2010..It is characterized by aggressive aneurysm formation and vascular tortuosity. We report the musculoskeletal demographic, clinical, and imaging findings of this syndrome to aid in its diagnosis and treatment...
Infantile restrictive cardiomyopathy resulting from a mutation in the cardiac troponin T geneStacie B Peddy
Department of Pediatric Cardiology, Johns Hopkins University School of Medicine, Baltimore, MD 21287, USA
Pediatrics 117:1830-3. 2006..She successfully received an orthotopic heart transplant 172 days after VAD implantation...
Fibulin-5 mutations: mechanisms of impaired elastic fiber formation in recessive cutis laxaQirui Hu
Department of Pediatrics, Washington University School of Medicine, St Louis, MO 63110, USA
Hum Mol Genet 15:3379-86. 2006..These findings support the hypothesis that fibulin-5 is necessary for elastic fiber formation by facilitating the deposition of elastin onto a microfibrillar scaffold via direct molecular interactions...
