Research Topics
| Fanny MochelSummaryAffiliation: CHU Dupuytren Country: France Publications
| Collaborators |
Detail Information
Publications
Pyruvate carboxylase deficiency: clinical and biochemical response to anaplerotic diet therapyFanny Mochel
Metabolic Unit, Departments of Pediatrics and Biochemistry, Hospital Necker Enfants Malades, Paris, France
Mol Genet Metab 84:305-12. 2005....
Energy deficit in Huntington disease: why it mattersFanny Mochel
Inserm UMR S975, Institut du Cerveau et de la Moelle, Paris, France
J Clin Invest 121:493-9. 2011..Here we review the clinical, biochemical, and molecular evidence of an energy deficit in HD and discuss the mechanisms underlying mitochondrial and related alterations...
Altered dopamine and serotonin metabolism in motorically asymptomatic R6/2 miceFanny Mochel
Inserm UMR S975, Institut du Cerveau et de la Moelle, Hopital de la Salpetriere, and Universite Pierre et Marie Curie, Paris, France
PLoS ONE 6:e18336. 2011..Therefore, we describe the earliest alterations of DA and serotonin metabolism in a HD murine model. Our findings likely underpin the neuropsychological symptoms at time of disease onset in HD...
Dietary anaplerotic therapy improves peripheral tissue energy metabolism in patients with Huntington's diseaseFanny Mochel
INSERM UPMC NEB, UMR S975, Centre de Recherche Institut du Cerveau et de la Moelle, Paris, France
Eur J Hum Genet 18:1057-60. 2010..A significant increase in serum IGF1 was also observed in all patients (205+/-60 ng/ml versus 246+/-68 ng/ml, P=0.010). This study provides a rationale for extending our anaplerotic approach with triheptanoin in HD...
Elevated CSF N-acetylaspartylglutamate suggests specific molecular diagnostic abnormalities in patients with white matter diseasesFanny Mochel
APHP, Department of Genetics, Hopital de la Salpetriere, Paris, France
Biochim Biophys Acta 1802:1112-7. 2010..In order to identify biomarkers useful for the diagnosis of genetic white matter disorders we compared the metabolic profile of patients with leukodystrophies with a hypomyelinating or a non-hypomyelinating MRI pattern...
Anaplerotic diet therapy in inherited metabolic disease: therapeutic potentialCharles R Roe
Institute of Metabolic Disease, Baylor University Medical Center, 3812 Elm Street, Dallas, TX 75226, USA
J Inherit Metab Dis 29:332-40. 2006....
